This site is intended for healthcare professionals

Go to /sign-in page

You can view 5 more pages before signing in

Clinical features

Authoring team

There is a spectrum of disease, but most commonly the patient presents aged between 1 and 4 years with:

  • progressive motor impairment - inability to walk, secondary to weakness
  • progressive mental deterioration
  • end stage disease is associated with quadriparesis, myoclonic seizures and nystagmus

There are juvenile and adult forms of this condition where onset is much later.


Create an account to add page annotations

Add information to this page that would be handy to have on hand during a consultation, such as a web address or phone number. This information will always be displayed when you visit this page